With the use of CRISPR gene editing technology, which disease has a treatment approved by the US Food and Drug Administration?
Sickle Cell Disease
|
|
4.5/5 |
Recently, two gene therapies for sickle cell disease were approved by the US Food and Drug Administration. It contains the first medication made possible by the ground-breaking CRISPR gene editing technique. For patients 12 years of age and older, both treatments were approved. The ground-breaking gene editing technique that earned its creators the 2020 Nobel Prize is used in the Vertex/CRISPR gene therapy.
More topics
Which organization publishes the 'Progress Report on the Twenty Point Programme'?
National Statistical Office
Which nations' navies recently participated in the Indian Navy's first trilateral exercise?
Indonesia and Australia.
What is the IUCN classification of the 'Gentoo Penguin' that was featured in the news recently?
Least Concern